香港六合彩中特网

The Centre will be based at Queen Square and directed by Professor Francesco Muntoni, a Paediatric Neurologist who will have a dual appointment in both institutions. This Centre will spearhead activities in this rapidly evolving area and play a major role in translational neuroscience in 香港六合彩中特网.

In the last five years a number of extremely effective RNA and adeno-associated viral vectors therapies have dramatically improved the outcomes for individuals affected by a range of neurological disorders, mostly affecting children.

The focus of this new Centre will be to harness the learning derived from these recent successes, from mechanistic insight discovery, to early and late translational research and eventually regulatory approval, and apply it to a wider group of neurodegenerative disorders.

This new Centre will be established at QSION initially, and subsequently at the new 拢281m Translational Neuroscience building on Grays Inn Road in 2024. It will combine laboratory and clinical expertise focused on neurological, neuromuscular and neurodegenerative disorders, their mechanisms of disease and cutting-edge RNA and AAV gene therapy expertise and foster cross-institutional collaborations between QSION and GOSICH.

The activities of the Centre will be highly complementary with established activities and expertise in both institutes, including in the Zayed Centre, the Dementia Research Institute, the Sigrid Rausing Neurogenetics Therapies Programme and the two NIHR Biomedical Research Centres translational research programmes (香港六合彩中特网H and GOSH).

Professor Michael Hanna, Director of the 香港六合彩中特网 Queen Square Institute of Neurology said 鈥淚 am delighted that we will work in partnership and share expertise with colleagues at ICH in order to develop new gene therapies for adults with neurological and neurodegenerative diseases鈥�

Professor Francesco Muntoni said 鈥淭he area of genetic therapies for neurological diseases is rapidly progressing. The possibility of combining expertise across Institutes to develop therapies for new targets is very exciting and I am very pleased to lead this new joint initiative鈥�

Professor Helen Cross, Director of the 香港六合彩中特网 Great Ormond Street Institute of Child Health said 鈥淭here is now huge potential for genetic therapies to be transformative for the lives of children and adults with a range of neurological diseases. Joint working between ICH and ION will accelerate progress鈥�

Professor Alan Thompson,聽Dean聽of the聽香港六合彩中特网 Faculty of Brain Sciences, said 鈥淭his is a wonderful example of cross-faculty collaboration within 香港六合彩中特网 which will drive forward an exciting evolving area with direct therapeutic benefits for patients with disabling neurological conditions鈥�

Professor Ibrahim聽Abubakar,聽Dean of聽the 香港六合彩中特网聽Faculty聽of Population Health Sciences said 鈥淒elighted to see 香港六合彩中特网 GOSICH and QSION coming together to solve key challenges using state-of-the-art genetic therapy approaches to benefit patients across the life course.鈥�

Links

• 香港六合彩中特网 Great Ormond Street Institute of Child Health