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Gene therapy may cure rare diseases but drugmakers have few incentives

21 June 2024

"This is a massive challenge and I'm not entirely sure we're going to be able to overcome it, but we have to give it a go because we've spent decades making these transformative treatments," outlines Professor Claire Booth (Ïã¸ÛÁùºÏ²ÊÖÐÌØÍø Great Ormond Street Institute of Child Health).

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